My name is  Therese Crutcher-Marin and I’m a Huntington’s Disease Advocate and Author.  Thank you for visiting my Author and Huntington’s Disease Advocate website.  I’m the President of the Huntington’s Disease Society of America San Francisco Bay Area Chapter.

What can we as a member of Huntington’s disease community do to move the approval of  UniQure AMT-130 from the FDA forward?  Here is a  way you can help.

1. Sign the petition below to the FDA

Urgent Call to Action for the HD Community 

Watch the video Announcement of the success of UniQure AMT-130 below

What the AMT-130 News Means for the HD Community

In this special HDSA Q&A session below, experts come together to discuss what these developments mean for families, caregivers, and advocates. Learn more about the latest updates, what’s next for the regulatory process, and how HDSA continues to support the community every step of the way.

AMT-130 What does it mean for the HD Community- Q&A

Below is Explanation from HDBUZZ.NET

Nov. 3, 2025 UniQure and FDA No Longer in Alignment on Approval Pathway for AMT-130

What is Huntington’s disease?  This picture shows the cruelest disease on the planet; Huntington’s disease and Juvenile Huntington’s disease.  Huntington’s disease is a hereditary disease that progressively damages nerve cells in the brain, leading to problems with movement, thinking, and behavior. It’s caused by a faulty gene and typically appears between the ages of 30 and 50, though it can occur earlier or later. There is NO CURE.

       

We Can Never Lose Hope…………………………